isth2015news.org
Gene Therapy Trial Takes Aim at Hemophilia B
Researchers may be making some headway in the search for a gene therapy strategy to treat hemophilia B. Preliminary findings from an ongoing phase 1-2 trial of an investigational gene therapy treatment to address clotting and immune response in patients with hemophilia B were presented Wednesday at the ISTH 2015 Congress. Previous research efforts to use