Vertex has done it!
It’s official! Vertex has finally found a way to treat the underlying problem with CF, instead of just treating side effects of this disease. With the combination of two pills, Kalydeco and VX-809, will now help repair the faulty CFTR protein in CF patients who have two copies of the deltaF508 gene! Basically, this will reverse lung damage. We will now be able to have increased lung function, increased weight gain, and decreased hospital admissions and pulmonary exacerbations.
They’re sending it to the FDA to be reviewed and given the thumbs up by the end of this year and hopefully be available for patients by 2015!
I have the the double deltaF508 gene, so I am beyond excited for this new medical advancement and can not wait to be able to try it for myself hopefully next year!!